1 |
Gene Therapy for selected Neuromuscular and Trinucleotide Repeat Disorders- An Insight to Subsume South Asia for Multicenter Clinical Trials |
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| | Nalaka Wijekoon, Lakmal Gonawala, Pyara Ratnayake, Darshana Sirisena, Harsha Gunasekara, Athula Dissanayake, Sunethra Senanayake, Ajantha Keshavaraj, Yetrib Hathout, Harry W.M. Steinbusch, Chandra Mohan, Ashwin Dalal, Eric Hoffman, K Ranil D de Silva | | | IBRO Neuroscience Reports. 2023; | | | [Pubmed] [Google Scholar] [DOI] | | 2 |
Serum fibroblast growth factor 21 and growth differentiation factor 15: Two sensitive biomarkers in the diagnosis of mitochondrial disorders |
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| | Akshata Huddar, Periyasamy Govindaraj, Shwetha Chiplunkar, Sekar Deepha, J.N. Jessiena Ponmalar, Mariyamma Philip, Madhu Nagappa, Gayathri Narayanappa, Anita Mahadevan, Sanjib Sinha, Arun B. Taly, Bindu Parayil Sankaran | | | Mitochondrion. 2021; 60: 170 | | | [Pubmed] [Google Scholar] [DOI] | |
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